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This week in gene and cell therapy - 15 February 2019

Gene and cell therapy headlines 11 - 15 February


Avrobio data for gene therapy for Fabry disease is looking up

Mixed results for Sangamo's first in vivo gene editing trial

Neurogene expands gene therapies for neurological and lysosomal storage diseases

Dosing started on Lysogene and Sarepta Therapeutics phase 2/3 trial of gene therapy for MPS IIIA (Sanfilippo)

Encouraging mid-way update from UniQure trial of gene therapy for haemophilia B